Gene therapy

Durham, N.C., Jan. 08, 2026 (GLOBE NEWSWIRE) — AB-1009 program advances to Phase 1/Phase 2; clinical trial initiated…

For most diseases, the challenge is not a lack of effort but the limits of existing tools and…

Science in 2026: what to expect this year Nature What to expect from 2026 in science, arts, politics and…

India’s Aditya-L1 spacecraft launched in 2023. Next year, it will observe the Sun during its peak activity phase.Credit:…

General Control enters Novo Nordisk’s Co-Creation Greenhouse to advance multiplex epigenetic editing for complex chronic disease. General Control,…

Feldman EL, Goutman SA, Petri S, Mazzini L, Savelieff MG, Shaw PJ, et al. Amyotrophic lateral sclerosis. Lancet.…

The malignant pediatric brain tumor medulloblastoma is driven by proteins deep within the cancer cells, for which there…

Altering a single gene may help people lower dangerously high levels of cholesterol and other fats in the…

“These findings highlight the potential of self-complementary AAVs to reduce dose requirements, minimize toxicity, and broaden clinical use…

Some genetic disorders-such as cystic fibrosis, hemophilia and Tay Sachs disease-involve many mutations in a person’s genome, often…

ADVERTISEMENT An experimental gene therapy has successfully treated dozens of children with a rare and fatal immune disorder,…

In a preclinical study, UC Davis Comprehensive Cancer Center scientists developed a highly targeted gene therapy that could…

AskBio Announces FDA Acceptance of Investigational New Drug (IND) Application for AB-1009 Gene Therapy for Treatment of Late-Onset Pompe Disease (LOPD)