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Browsing Tag

Leber Congenital Amaurosis

1 post
HHealth
New generation of CRISPR shows safer path to treating genetic diseases
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Retinal organoids provide a powerful tool to diagnose and study Leber congenital amaurosis

  • December 4, 2025
Leber Congenital Amaurosis (LCA) is an inherited retinal disease leading to severe vision impairment from early infancy, affecting…
Ireland
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