Creating bottom-up RNA transfer vehicles from synthetic protein assemblies
Molecular cloning All cloning was performed using standard molecular techniques. Fragments for cloning were generated by PCR using…
Louisiana Notches a Sickle Cell First
A 23-year-old from suburban New Orleans may have just opened a new chapter in how Louisiana treats…
Scottsdale couple raises millions to fight blindness | Neighbors
When Dr. Stephen Johnston and his wife, Kristina, learned their young son would likely lose his sight, the…
Regeneron (REGN) Says EMA Accepted Review for Otarmeni Application
Regeneron Pharmaceuticals, Inc. (NASDAQ:REGN) is one of the 10 Best Debt-Free S&P 500 Stocks to Buy Now. On…
Multicentre gene therapy for OTOF-related deafness followed up to 2.5 years
Yasunaga, S. et al. A mutation in OTOF, encoding otoferlin, a FER-1-like protein, causes DFNB9, a nonsyndromic form…
UTSW Spinout InterAct Therapeutics Selected by Cell & Gene Therapy Incubator Program » Dallas Innovates
Left: Daniel Hargrove, co-founder and CEO of InterAct Therapeutics; Right: Isaac Chan, MD, PhD, Co-founder and CSO of…
CRISPR gene editing therapy cuts LDL cholesterol in small study
A CRISPR-based gene editing therapy dramatically reduced levels of low-density lipoprotein, often called “bad cholesterol,” and triglycerides in…
uniQure Provides FDA Update on AMT-130; BLA Timing Unclear
uniQure (NASDAQ: QURE) on Nov. 3, 2025 announced FDA feedback…
New gene-editing method can correct many disease-causing mutations in mammalian cells
Some genetic disorders-such as cystic fibrosis, hemophilia and Tay Sachs disease-involve many mutations in a person’s genome, often…
Next-generation gene therapy tools built by UH scientist
Reading time: 2 minutesAssistant Professor Jesse Owens using a program to model the structure of his integrase protein.…